Biotechnology company United Therapeutics Corporation (Nasdaq:UTHR) said on Monday that the US Food and Drug Administration (FDA) has accepted its New Drug Application for ralinepag to treat pulmonary arterial hypertension (PAH), setting a Prescription Drug User Fee Act target action date of 24 June 2027.
If approved, ralinepag would be the first and only once-daily oral prostacyclin for PAH, according to the company.
The filing is supported by Phase 3 ADVANCE OUTCOMES data, in which ralinepag reduced the risk of clinical worsening by 55% versus placebo in predominantly pre-treated PAH patients. Ralinepag also reduced NT-proBNP levels, improved exercise capacity and increased the odds of clinical improvement by 47%.
The results were consistent across patient subgroups, including disease etiology, six-minute walk distance, WHO Functional Class, NT-proBNP levels and background therapies.
United Therapeutics said ralinepag's safety profile was consistent with known prostacyclin-related adverse events, with no new safety signals identified.
Ralinepag remains investigational and has not been approved by the FDA for any indication.
Guardant Health wins FDA approval for Guardant360 CDx in advanced breast cancer
Agilent launches S540MD slide scanner system in US
Kali Therapeutics' KT501 Investigational New Drug application cleared by US FDA
NeuroSense reveals strategy to advance PrimeC toward potential ALS approval
UCB agrees with US government to lower medicine costs and strengthen US manufacturing
Karyopharm seeks accelerated FDA approval for selinexor–ruxolitinib in myelofibrosis