Interim data has been selected for an oral presentation at the upcoming L...
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Green Cross obtains approval in Korea for Hunter syndrome drug
Life Technologies forms JV with Chinese DaAn Gene for molecular diagnostic assays
Health Canada places Cinryze under Priority Review status
CSL Behring starts Phase II/III trial in haemophilia patients
Merck Serono launches validation study of PKU-QOL questionnaire
MDA grants Tivorsan USD1m to advance clinical work on DMD treatment
Prana gets FDA nod to initiate study of PBT2 in Huntington's disease
Biogen Idec, Isis form partnership for SMA antisense programme
Synageva completes enrollment in Phase I/II study of SBC-102 for LAL Deficiency
Amicus Therapeutics completes enrolment in Phase III study of migalastat HCl
Selexys finalises Phase I trial for sickle cell compound
Baxter's ADVATE gets FDA approval for prophylaxis of Hemophilia A in adults, children
Michael Kelly joins Cure Duchenne as chief scientific officer