Therapy Areas: Hereditary Disorders
15 February 2024 - Clinical-stage gene editing company Intellia Therapeutics Inc (NASDAQ:NTLA) and ReCode Therapeutics, a clinical-stage genetic medicines company, announced on Thursday a strategic co...
25 January 2024 - Sionna Therapeutics, a US-based life sciences company, announced on Wednesday that it has dosed its first healthy subject in a phase one clinical trial of SION-109 involved in develo...
27 November 2023 - Late-stage clinical mRNA medicines company Arcturus Therapeutics Holdings Inc (Nasdaq: ARCT) announced on Monday that it has received Orphan Drug Designation from the U.S. FDA for A...
7 September 2023 - SpliSense, an Israel-based biopharmaceutical company, announced on Wednesday that it has completed a first-in-human, Phase one clinical trial of SPL84, the company's lead inhal...
1 September 2023 - Alcresta Therapeutics, Inc., a US-based commercial-stage company involved in developing and commercialising novel enzyme-based products, announced on Thursday that the US FDA has ap...
10 August 2023 - - US-based Vertex Pharmaceuticals Inc. (NASDAQ: VRTX) has announced publication in the New England Journal of Medicine (NEJM) of preclinical data and the results from i...
Related Headlines