Intellia Therapeutics and ReCode Therapeutics join forces for gene editing therapies in cystic fibrosis

Sionna Therapeutics doses first healthy subject in SION-109 phase one clinical trial

Arcturus Therapeutics granted FDA Orphan Drug Designation for ARCT-032 to treat cystic fibrosis

SpliSense completes SPL84 first-in-human, Phase one clinical trial for cystic fibrosis treatment

Alcresta Therapeutics' RELiZORB (iMMOBILIZED LIPASE) cartridge receives FDA expanded use clearance for paediatric patients aged 2 to 5 years

Positive Phase 2, Proof-of-Concept Results for VX-548 Published in New England Journal of Medicine

Inogen acquires Physio-Assist, expanding respiratory product portfolio and global presence

Vertex Pharmaceuticals receives European Commission approval for ORKAMBI (lumacaftor/ivacaftor) To treat children with cystic fibrosis aged 1 to <2 years old

cystetic Medicines doses first healthy volunteer in CM001 Phase one clinical trial

Vertex Presents Data Demonstrating Significant Benefits of Long-Term Treatment with CFTR Modulators at the European Cystic Fibrosis Conference

First Patient Enrolled in Phase 3 Clinical Trial Evaluating ARINA-1 in Lung Transplant

Vertex and CRISPR Therapeutics Complete Submission of Rolling Biologics License Applications to the US FDA for exa-cel for the Treatment of Sickle Cell Disease and Transfusion-Dependent Beta Thalassemia

Insmed completes adult patient enrolment in brensocatib pivotal ASPEN study

Vertex Receives FDA Clearance of Investigational New Drug Application for VX-264, a Novel Encapsulated Cell Therapy for the Treatment of Type 1 Diabetes

Aluna Raises USD 15.3m in Series B Funding