Japan-based late-stage clinical biopharmaceutical company Renalys Pharma, Inc. announced on Monday that sparsentan, licensed from Travere Therapeutics, Inc., has received Orphan Drug Designation in Japan for primary IgA nephropathy.
Designation by the Japanese Ministry of Health, Labour and Welfare applies to conditions affecting fewer than 50,000 patients with high unmet medical needs, offering benefits such as priority review and a potentially faster approval timeline.
Sparsentan, already approved in Europe and the United States, is undergoing phase III clinical trials in Japan using data from the global PROTECT study. Renalys Pharma holds exclusive development and commercialization rights for sparsentan across Japan and multiple Asian markets. Efforts will focus on addressing the critical need for effective treatment options for IgA nephropathy, a leading cause of kidney failure.
Travere Therapeutics received FDA approval in September 2024 for sparsentan under the US brand name FILSPARI. The drug is designed to slow kidney function decline in patients with high-risk IgA nephropathy progression. Renalys Pharma remains committed to expediting sparsentan's availability to patients in Japan.
Diamyd Medical agrees accelerated efficacy readout in ongoing Phase 3 type 1 diabetes trial
INOVIO's INO-3107 Biologics License Application accepted by US FDA
ABL Bio receives upfront payment and equity investment from Eli Lilly
CARsgen Therapeutics submits two IND applications for CT0596 to Chinese regulator
Repare Therapeutics sells RP-3467 asset to Gilead Sciences for up to USD30m
Sanofi agrees USD2.2bn acquisition of Dynavax to strengthen adult vaccine portfolio
Sanofi and Regeneron's Dupixent gains Japan approval for paediatric asthma patients aged 6 to 11
Aqualung Therapeutics' Phase 2a lung fibrosis study approved by US FDA
NeuroSense Therapeutics completes safety evaluation of PrimeC in Alzheimer's Phase 2 study
BrioHealth Solutions enrols 100th participant in BrioVAD System trial
Faron launches BLAZE trial with Institute of Cancer Research to address immunotherapy resistance
AstraZeneca secures US Breakthrough status for Enhertu in early breast cancer
Ipsen licenses Simcere Zaiming antibody-drug conjugate for global development